Design Therapeutics

Design Therapeutics

Biotechnology Research

Carlsbad, CA 2,087 followers

About us

We are a clinical-stage biotechnology company developing a new class of therapies based on its platform of GeneTAC™ gene targeted chimera small molecules. The company’s GeneTAC™ molecules are designed to either dial up or dial down the expression of a specific disease-causing gene to address the underlying cause of disease. Design’s lead program is focused on the treatment of Friedreich ataxia, followed by programs in Fuchs endothelial corneal dystrophy and myotonic dystrophy type-1 and discovery efforts for multiple other serious degenerative disorders caused by nucleotide repeat expansions. For more information, please visit designtx.com.

Industry
Biotechnology Research
Company size
51-200 employees
Headquarters
Carlsbad, CA
Type
Public Company
Founded
2017

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