Ascidian Therapeutics’ Post

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We invite you to tune in to "Rare Insights" on Monday July 29th to hear from our own Dr. Jay Barth about all things #RNAExonEditing and our groundbreaking lead program in #StargardtDisease. Thanks for providing your insights, Jay, and thank you Taren Grom and Know Rare for sharing important information about RNA editing in rare disease research.

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Ready for a deep dive into RNA editing? 🎙️ 💭     Join us for episode 2 of "Rare Insights" where host Taren Grom sits down with Dr. Jay Barth, Chief Medical Officer at Ascidian Therapeutics.    Discover how “sea squirts” are inspiring groundbreaking RNA editing technology for rare diseases! 🧬✨    Dr. Barth shares insights on:    1️⃣ Ascidian’s innovative RNA exon editing.  2️⃣ Minimizing risks in gene editing.  3️⃣ Fast-track FDA designation for Stargardt disease treatment.  4️⃣ The rise of RNA editing in rare disease research.  5️⃣ His inspiring career journey in the rare disease field.    Don't miss “Rare Insights: 2 Using “Sea Squirts” to rewrite RNA with Ascidian Therapeutics” dropping on July 29th!    Catch up on all our episodes on Apple Podcasts, Spotify, or your favorite podcast player.     Just search "Rare Insights." 🔎      -    #RNAediting #medicalresearch #rarediseaseawareness #medicalpodcasts #clinicaltrials #clinicalresearch #clinicaltrial #KnowRare #RareInsightsPodcast

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