American Society of Gene & Cell Therapy’s Post

i will like to share article about clinical trials Rare disease #clinicaltrials #clinicaltrial #clinicalresearch #raredisease

NTAP Coding Challenge: Sickle Cell Disease Treatment Provides New Hope Imagine living in fear that your next episode of severe pain could happen today. You want to do something fun like hiking on a beautiful mountain or sledding down a snowy hill but you know you can’t. That’s because cold and higher altitudes with lower oxygen concentrations are just two of the many things that can trigger a sudden, severe episode of vaso-occlusive crisis in patients with severe sickle cell disease, keeping them from enjoying many things that others do with ease. Click the link below to read the complete article.

Did you know it is World Parkinson’s Day? We'd like to share some of our key articles which highlight how far we've come in #Parkinson's research! Identifying Parkinson’s Inhibitors | https://bit.ly/3vNrtOm Parkinson’s Disease Diagnosis Goes Skin Deep | https://bit.ly/33iNHGL Parkinson’s Progress | https://bit.ly/3PSYhM4 #WorldParkinsonsDay #Parkinsonsday

Successful clinical trials in ALS must account for the many challenges the nature of the disease presents to research. From controlling for disease heterogeneity to overcoming diagnostic delays, check out these considerations for your trial. We’re committed to advancing ALS treatments and raising #ALS Awareness. Read more in our blog: https://ow.ly/uJkW50RT9B0

September is National Sickle Cell Awareness Month, a good time for #coding professionals to familiarize themselves with the disease and the different codes to use depending on the type of #SCD. https://lnkd.in/gxuAspFq #PCGnews #medicalcoding

🔬Explore the power of #PrecisionMedicine for the future of disease therapies utilizing ultra-sensitive #epigenomics - like CUT&RUN and CUT&Tag - in our blog. https://hubs.la/Q02vSN2t0 🧬

New clinical study to advance development of treatments for liver cirrhosis: The £30m ADVANCE study is the most extensive study into liver disease worldwide #News #AcceleratingDiscoveryActionableNASHCirrhosisEndpoints

🔍 Myeloma Patients Europe (MPE) has put together a Q&A resource to explain the key distinctions between myeloma and AL amyloidosis. 📚 Learn more about symptoms, diagnosis, treatment and more in this detailed guide: 👉: https://lnkd.in/dptDc5AN #ALAmyloidosis #Myeloma 

Some great insights from rare disease patients that highlight key considerations for sponsors in clinical trials. Discover what matters most to these individuals and how sponsors can enhance the clinical trial experience. Valuable perspectives shaping the future of rare disease research! #ClinicalTrials #RareDiseases #PatientPerspective