🧬At our recent event, we showcased additional Stargardt disease Phase 2 results that shows the potential of Tinlarebant to slow or halt lesion growth. In the 24-month study, 42% of patients with ABCA4 mutations saw no new atrophic lesions and maintained stable QDAF levels. #Tinlarebant #StargardtDisease https://lnkd.in/gf_8ny_W
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Efficacy and safety of zibotentan and dapagliflozin in patients with chronic kidney disease: study design and baseline characteristics of the ZENITH-CKD trial Evaluate the effect of combination zibotentan/dapagliflozin versus dapagliflozin alone on albuminuria and estimated glomerular filtration rate (eGFR). https://lnkd.in/dbEwzCr5
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R&D Stepping Up: Redifining risk factors diabetes, cardiac and liver diseases. Phenome India and ambitious project. A longitudinal study is being conducted to develop an enhanced prediction model for diabetes, cardiac and liver disease. https://lnkd.in/d_yssjFZ #R&D #India #CSIR #Research #Modeling #Predictionmodel
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Creative, grateful, resilient, and honest physician-scientist driven by an unwavering passion for the fight against diabetes.
Enjoy our latest review article on the role of T cell trafficking in chronic autoimmune diseases and dysmetabolisms now out in iScience #Tcell #recirculation #diabetes #metabolicdisorders #autoimmunity https://lnkd.in/di8RUh5K
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Explore an up-to-date account of the diverse molecular mechanisms and the causal role that fibrosis plays in disease progression (contributing to and exacerbating dysfunction of affected organs). Read our latest themed issue now: https://ow.ly/buk850Q5soc #Fibrosis #TherapeuticTarget #Necroptosis #LiverDisease #GProtein #CardiacFibrosis #KidneyFibroblasts
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More congenital hyperinsulinism news! Recent findings suggest that a 2.4Mb deletion on chromosome 20p11.2 causes HI through the disruption of FOXA2. Find out more at: https://lnkd.in/eSrF6vWt #hyperinsulinism #raredisease #congenitalhyperinsulinism #hypoglycemia | Hyperinsulinism | Congenital | HI | Hypoglycemia | Rare Disease
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September 24 is Familial Hypercholesterolemia (FH) Awareness Day. FH is one of the most common genetic condition that causes high cholesterol. It is not caused by the food you eat, it is a family condition. Millions of people around the world don't know they and their families are at risk for early heart disease, heart attacks, stroke, and even death. With better awareness and early diagnosis, those with FH can reduce their risk for heart disease by 80% If you suspect you have FH, please consult your healthcare provider or find a lipid specialist. #FHAwarenessDay #FHAwarenessDay2023 #KnowFH #FH #FamilialHypercholesterolemia #Cholesterol
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Join us in spreading awareness about Thalassaemia, a hereditary disorder that affects the production of hemoglobin, leading to reduced red blood cell count and anemia. With an estimated 100 million people worldwide carrying genes responsible for thalassaemia and more than 300,000 babies born annually with severe forms of this disease, World Thalassaemia Day is a call to raise awareness about this condition and its impact while at the same time extending solidarity with thalassemia community worldwide. Your strength inspires us all. #YouInspireUs #Zydus #ZydusLifesciences #Thalassemia #ThalassaemiaDay2024 #WorldThalassaemiaDay #WorldThalassaemiaDay2024 #Blood #BloodDisorder #Screening #Prevention #SafeTransfusion
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Hereditary Angioedema (HAE) is a rare and potentially life-threatening genetic disease that occurs in about 1 in 10,000 to 1 in 50,000 people. HAE symptoms include edema (swelling) in various body parts, including the hands, feet, face, and airway. Because the disease is very rare, it is not uncommon for patients to remain undiagnosed and often suffer for many years. To learn more about this disease, the treatments available, and how to recognize early warning signs, visit https://lnkd.in/g7VZTQRc #HAE #HAEawareness
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Hereditary Angioedema (HAE) is a rare and potentially life-threatening genetic disease that occurs in about 1 in 10,000 to 1 in 50,000 people. HAE symptoms include edema (swelling) in various body parts, including the hands, feet, face, and airway. Because the disease is very rare, it is not uncommon for patients to remain undiagnosed and often suffer for many years. To learn more about this disease, the treatments available, and how to recognize early warning signs, visit https://lnkd.in/g7VZTQRc #HAE #HAEawareness
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Long-term exposures to radioactivity and inhalation of radionuclides have serious health effects such as chronic lung diseases, acute leucopoenia, anemia and necrosis of the mouth. Exposure to radium may result in teeth fracture, anemia and cataract and may even cause cancer of various types. https://lnkd.in/dRCFwBtE › pii Evaluation of excessive lifetime cancer risk due to natural ... if there's a lithium rush...
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Orthopaedic Surgeon
3moAny time line for launch of drug in market for patients..??