Grand Strand Clinical Trial Services, LLC’s Post

As you may have heard by now, the FDA is continuing to take steps to advance treatments for rare disease. The CBER and CDER together have initiated the START Pilot Program which allows chosen companies with rare disease treatment options to have easier access to FDA support, guidance, and initiatives. Among the rare diseases being studied are: Friedrich's ataxia, Vanishing White Matter disease, Sanfilippo syndrome, NGLY1 Deficiency, Isolated methylmalonic acidemia, Canavan Disease, and Rett Syndrome. We are looking forward to seeing the progress made through the START Pilot Program! #clinicalresearch #innovation #FDA #STARTpilotprogram #gsclinical

FDA Opens Doors for More Treatments for Rare Diseases

FDA Opens Doors for More Treatments for Rare Diseases

fda.gov

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