#podcast Nolan Townsend, CEO of Lexeo Therapeutics, and Jen Farmer, CEO of FARA, the Friedreich's Ataxia Research Alliance, are working together to better understand and treat Friedreich's Ataxia. This rare genetic condition includes cardiomyopathy and scoliosis. Lexeo Therapeutics is studying gene therapy as a potential treatment for the cardiovascular component of the disease. The Friedreich's Ataxia Research Alliance (FARA) plays a role in funding research, understanding the natural history of the disease, and advocating for treatments. #FriedreichsAtaxia #CureFA #FAAwarenessMonth #FAAwarenessDay #RareDiseases LexeoTX.com CureFA.org https://lnkd.in/g94V2-Pz
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Cell and gene therapies (CGT), also known as “Advanced Therapy Medicinal Products” (ATMP), address diseases by directly repairing genetic defects within the body or introducing tissues or cells with new functions. These innovative therapies can correct or cure a wide range of conditions. The development and manufacture of these medicines are complex and novel, and they have only recently started gaining traction in the commercial sphere over the past decade. What sets them apart is their remarkable potential to offer permanent cures rather than temporary symptom reduction. Get an overview in the latest article by VTU experts Cornelia Haas and Birgit Krenn, which appeared in the magazine “botenstoff” of the Human.technology Styria GmbH (February 2024 issue, Precision Medicine special edition). #VTU #CellandGeneTherapy
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Are you testing therapeutics for ocular toxicity? See how retinal pigment epithelium models can be used to investigate efficacy of gene therapy vectors on both healthy and patient-derived tissues [ link to https://lnkd.in/eQxtFhrf] Speak to our experts to accelerate your research.
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The “hf” in hfCas12Max stands for high-fidelity, and it’s not just a label—it's fact. hfCas12Max surpasses other common CRISPR nucleases by delivering high on-target editing with minimized off-target editing, which is critical for developing precise and effective #crispr -based cell and gene therapies. See for yourself how hfCas12Max is the right nuclease for you: https://lnkd.in/g7FjR7Gf
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Souad Messahel, PhD, Elpida Therapeutics on Clinical Trials in Rare Diseases - Strategies for Resource Management, exploring the development costs for a biotech for a gene therapy. #ASGCT24, within the “Why Do Rare Disease Clinical Trials Often Miss The Mark” workshop
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Advancing cell and gene therapies (CGTs) globally presents unique hurdles at every step, and Labcorp has the experience and capabilities to help you overcome them. In a recent presentation for the Korea Biomedicine Industry Association (KoBIA), Maryland Rosenfeld Franklin, PhD, vice president and enterprise head of CGT at Labcorp, discussed some of these challenges and explored their solutions. Watch the recorded webinar to learn more. #CellandGeneTherapy #CellTherapy #GeneTherapy
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Associate Director, Proposal Management at Labcorp | Early Development | Enterprise Client Solutions
Advancing cell and gene therapies (CGTs) globally presents unique hurdles at every step, and Labcorp has the experience and capabilities to help you overcome them. In a recent presentation for the Korea Biomedicine Industry Association (KoBIA), Maryland Rosenfeld Franklin, PhD, vice president and enterprise head of CGT at Labcorp, discussed some of these challenges and explored their solutions. Watch the recorded webinar to learn more. #CellandGeneTherapy #CellTherapy #GeneTherapy
ON-DEMAND WEBINAR: Key challenges and lab solutions in your global cell and gene therapy trials, Mar. 20, 2024 | Labcorp
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This Cystic Fibrosis Awareness Month, read MERIT's article to learn more about CFTR modulators and gene therapy treatments for rare mutations. https://lnkd.in/dvG994Eb #CysticFibrosis #respiratory #clinicaltrials #CysticFibrosisAwarenessMonth
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Senior Business Development Director | Partnering with Biotech & Pharma on Non-Clinical Safety & DMPK
Advancing cell and gene therapies (CGTs) globally presents unique hurdles at every step, and Labcorp has the experience and capabilities to help you overcome them. In a recent presentation for the Korea Biomedicine Industry Association (KoBIA), Maryland Rosenfeld Franklin, PhD, vice president and enterprise head of CGT at Labcorp, discussed some of these challenges and explored their solutions. Watch the recorded webinar to learn more. #CellandGeneTherapy #CellTherapy #GeneTherapy
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Advancing cell and gene therapies (CGTs) globally presents unique hurdles at every step, and Labcorp has the experience and capabilities to help you overcome them. In a recent presentation for the Korea Biomedicine Industry Association (KoBIA), Maryland Rosenfeld Franklin, PhD, vice president and enterprise head of CGT at Labcorp, discussed some of these challenges and explored their solutions. Watch the recorded webinar to learn more. #CellandGeneTherapy #CellTherapy #GeneTherapy
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Osteoarthritis, one of the most common and debilitating chronic diseases, affects more than 30 million Americans, a number that is expected to increase exponentially as the population ages. Therapeutic options are limited. Current approaches start with nonpharmacological treatments such as walking aids, weight loss, and physical therapy, followed by acetaminophen and NSAIDS. Pioneers working on gene therapies for osteoarthritis and other chronic joint conditions won the prestigious OREF Award for 2024 at this year’s AAOS. One of the winners, Christopher Evans, PhD, discusses 30 years of research leading up to the founding of Genascence Corporation, which is now in clinical trials for a gene therapy for OA: https://bit.ly/3VDAh3R #medtech #osteoarthritis #chronicdisease #jointcondition #genetherapy
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