Ludovic Helfgott’s Post

Yesterday, I joined the 37th EURORDIS-Rare Diseases Europe ERTC Workshop panel discussion, and I wanted to share some of the things that stuck with me. We drilled into how we can improve access to #RareDisease treatments in Europe - a critical task requiring collective action to ensure treatments reach patients: 1️⃣ Innovation: We must stimulate more breakthrough and incremental innovation. 2️⃣ Collaboration: Trust and new thinking are crucial to define flexible approval, access pathways, and evidence requirements to drive innovation. 3️⃣ Policy: More flexible, patient-centred regulatory frameworks and reimbursement models that account for the cost of care versus the cost of treatment are needed. Let's keep working together as a community to ensure everyone gets access to the treatment they need when they need it. #HealthCareInnovation

Today’s 37th Workshop of the #EURORDIS Round Table of Companies saw over 130 registrants, representing 19 countries, gather to discuss the importance of transforming foresight into action to support the development of affordable and accessible treatments for rare diseases patients! 🗣️ Here are the key learnings: - Early dialogues between patients, regulators, HTA bodies, payers, and developers are key to fostering innovation. Check out our recommendation for an orphan drug development plan: https://lnkd.in/eSQWhn9Z - Mechanisms such as PRIME and MoCA are important examples of these collaborations but trust must remain at the heart of these relationships in order to foster the type of changes we want to see. - To overcome global healthcare challenges and reach the goal of 1000 new treatments by 2030, we as a community must continue to drive change and turn good will into action. Transparent public-private relationships between patient advocates, industry, academia and decision makers are essential to shape policies that best serve the interests of our community. Learn more about the ERTC on our website. Tomasz Grybek, Kevin Loth #collaboration #industry #relationships #workshop #cooperation #meeting

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