MTF Biologics’ Post

DONATE TO THE MSA DRUG REPURPOSING EXPLORATORY FUND: www.defeatmsa.org/donate ~ Choose the MSA Drug Repurposing Fund - Thank You for the Donation! #defeatmsa #kickmsa #msawarriors #newdrugs #clinical #msaresearch #clinicalresearch #repurposing #drugs ~ About the Cure Parkinson’s UK iLCT Program, a pioneering drug repurposing program for Parkinson’s - explained by Dr Patrik Brundin: https://lnkd.in/gMW86-7f

ABC is asking where our plasma comes from and the ethical conundrum of filling gaps in supply from international markets with paid donors while only supporting non remunerated donations. While plasma is processed for a high degree of safety, we cannot discount the importance of donor selection in blood safety, and if deferral means your children go without, donors will accept a higher risk. Where I think there will be most agreement is understanding who really does benefit most from immunoglobulin therapy and identification promotion alternatives. Needs more in transfusion research. https://lnkd.in/dcZxytd5

● Pharma with Miremad ○ Blood vs. Plasma number of donations in the year? #plasma #donation #donations #Pharma #blooddonation #marketanalysis #marketreports #blooddonor #pharmawithmiremad

For more information about the studies above and eligibility requirements, please see below:  1. A Phase 3 Study of Rusfertide in Patients With Polycythemia Vera (Protagonist Therapeutics, Inc.  # PTG-300-11) - https://shorturl.at/bsIJ9 2. A Study of Bomedemstat (MK-3543) in Participants With Polycythemia Vera (MK-3543-004) (Imago BioSciences, Inc., a subsidiary of Merck & Co., Inc., (Rahway, New Jersey USA) #MK-3543-004) - https://shorturl.at/cixL4 3. Study to Assess SLN124 in Patients With Polycythemia Vera (Silence Therapeutics plc #SLN124-004) - https://shorturl.at/gvzH2 Be the first to know about which clinical trials are recruiting by signing up for our mailing list at https://lnkd.in/gCTN_pf3 and take action with us towards finding better treatments and eventually a cure for ET, PV, and MF by donating today:

📣 BIG NEWS! Together with our enabling partners Amgen, Global Focus on Cancer (US charitable organisation supported by donations from Eli Lilly and Company), MSD, Roche, Siemens Healthineers and others, this morning on the #CGI2024 Clinton Global Initiative world stage, C/Can proudly launched a bold, new 7-year, $10M initiative to help address the widening #CancerCare gap among women living in resource-limited settings in low- and middle-income countries. Because neither where a person lives, nor their gender, should impact the quality of the care they receive. 🙌 Developed in response to findings of the Women, power, and cancer: The Lancet Commission and informed by our Advisory Board of women in these countries, this new strategy uses our proven city model to shape interventions that meet the unique needs of local populations, while centring #GenderEquity. Learn more and get involved: https://lnkd.in/d7w7MzhD #UNGA79

How to donate umbilical cord blood (https://lnkd.in/gVw98znS) Traditionally, umbilical cord blood has been discarded as medical waste. In recent years, mothers also have had the option to bank their cord blood for family use – at a cost. Now thanks to the California Umbilical Cord Blood Collection Program, mothers can donate their newborns' umbilical cord blood for public use in lifesaving transplantations or research, at no cost to themselves or their insurance. All mothers giving birth at a participating hospital will be offered the opportunity to donate if staff is present and certain criteria are met, similar to the criteria for donating blood. The cord blood collection does not interfere with the birth plan and is safe for mom and baby, occurring after the birth.

Imagine a prescription drug that you need to maintain your quality of life coming with a price tag of $900....a day. Last week, I had the pleasure of meeting Lauren, a woman in her 30s living with cystic fibrosis. Lauren gave me a glimpse into the life of someone living with this disease. She shared the various tools and machines that can be used to keep her lungs and airways clear, as well as her drug regimen to help treat the symptoms that come with cystic fibrosis. One of those drugs was a game changer for many – though not all – living with cystic fibrosis when it came on the market several years ago. It's comprised of 3 pills that need to be taken daily. Without insurance or financial assistance, EACH pill’s list price can be about $300. Here's some quick math: -$300/pill x 3 pills/day = $900/day -$900/day x 365 days/year = $328,500/year This really put several things into perspective for me: 1) The need for prescription drug costs to be more closely monitored and controlled, down to the manufacturer level. We've seen similar stories with things like EpiPens and insulin. 2) The importance of making sure everyone has access to affordable health care and that those who may need it can use financial assistance programs to help cover their costs. 3) The critical need of finding a cure for diseases like cystic fibrosis, so that individuals don't need to rely on these drugs to try and manage their health. You can have a direct impact on number 3 – please consider donating using the link below.  Every dollar is one dollar closer to making that a reality! https://lnkd.in/gKFhB_9X And don’t forget that I’m “Climbing for a Cause” at the end of August – you can make a future donation commitment for each time I summit Bristol Mountain.  Simply comment below or message me directly with your commitment amount.

💙 Niccolo (20), Alessandro (13) and Sammy (28) are among nearly 100 children & young adults with #Progeria across the world who are benefitting from the life-extending, FDA-approved lonafarnib drug. PRF will continue to devote funds to ensure access to lonafarnib for all, and to study its long-term effects. But we won’t stop there. PRF is exploring 3 other therapeutic pathways to treat and cure Progeria, attacking this disease: at the Protein, at the RNA and at the DNA levels. 💙 Donate here: https://bit.ly/OPTeamPRF 💙 The Progeria Research Foundation is dedicated to making sure all children & young adults with Progeria have a bright future. Thanks to YOU, PRF continues to make a dramatic impact on the length and quality of life for those with Progeria. Please continue your vital support and be ONE who makes the cure POSSIBLE! #ONEpossible #fundraiser #fundraisingcampaign #research #scientificbreakthroughs #lonafarnib #progerin

For anyone that has suffered from pushing the document and data regulatory boulder uphill, only to have to do it again the next day, same path, same grind, crying out in your head (because to do so at work would get you a visit from HR) "please, God!! There has GOT to be a better way than this!!" What's great about Accumulus Synergy: It's not regulatory operations business as usual. It's a creative, strategic, collaborative solution to the crushing boot of inefficiency in the typical regulatory process. Bravo and best of luck! This is clearly a space where creative innovation is needed.

Moving forward the transformation of the regulatory filing process globally