On Tuesday, July 9, management will participate in the BMO 2024 Genetic Medicines Summit. To learn more, read our full press release here: https://bit.ly/3L68OBx
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For the most part, the technology used to treat #Duchenne muscular dystrophy has been focused on exon skipping. But as is the case with many boys with the condition, my son Caffrey's mutation is not amenable to this type of treatment. That’s why we need to continue to develop additional therapeutic options for #DMD. Thank you, Rare Disease Advisor, for the opportunity to share Caffrey’s story and how his diagnosis helped me appreciate the sheer unmet medical need there is not only within the Duchenne community, but also broadly across all #rarediseases – and what we are doing at @Alltrna to accelerate #raredisease #drugdevelopment.
Alltrna’s CEO Michelle Werner discusses with Larry Luxner of Rare Disease Advisor her personal and professional mission to accelerate #raredisease #drugdevelopment and how new tRNA genetic medicines could do this: by treating many diseases at once. 🎧 Listen to the interview: https://lnkd.in/gStF48fc #tRNA #RNA #tRNAmedicines #tRNAbiology #rarediseases #StopCodonDisease #geneticmedicines #programmablemedicines
Alltrna's Michelle Werner Interviewed for Rare Disease Advisor
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Unveiling the power of pharmacogenomics! Discover how genetic testing with #BHGlab can tailor medication prescriptions for better patient outcomes. #PrecisionMedicine #HealthcareRevolution
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A Mechanisms of Kidney Diseases article stresses why genetic testing is of significant clinical benefit to many patients with CKD, provides recommendations for which patients to test, and gives guidance on interpretation of testing results Journal of the American Society of Nephrology 35(8):p 1107-1118, August 2024 DOI: 10.1681/ASN.0000000000000401
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Access the newest article from Pharma insights! Learn how RGD peptide-based lipids are revolutionizing mRNA delivery, offering targeted precision and enhanced efficacy in treating genetic disorders. Click here: https://ow.ly/MSIs30sCfSz #CrodaPharma #EmpoweringBiologicsDelivery #PharmaInsights
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Access the newest article from Pharma insights! Learn how RGD peptide-based lipids are revolutionizing mRNA delivery, offering targeted precision and enhanced efficacy in treating genetic disorders. Click here: https://ow.ly/1wVi30sCgna #CrodaPharma #EmpoweringBiologicsDelivery #PharmaInsights
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Access the newest article from Pharma insights! Learn how RGD peptide-based lipids are revolutionizing mRNA delivery, offering targeted precision and enhanced efficacy in treating genetic disorders. Click here: https://ow.ly/y73K30sCiBH #CrodaPharma #EmpoweringBiologicsDelivery #PharmaInsights
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Access the newest article from Pharma insights! Learn how RGD peptide-based lipids are revolutionizing mRNA delivery, offering targeted precision and enhanced efficacy in treating genetic disorders. Click here: https://ow.ly/BBpf30sColG #CrodaPharma #EmpoweringBiologicsDelivery #PharmaInsights
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Did you miss the recent Devyser webinar with Dr. Robert Akkers highlighting the shifting distribution of hemoglobinopathy, and the need for expanded thalassemia genetic testing? Now watch the on-demand webinar here: https://hubs.ly/Q029zDBX0 #thalassemia #ngs #genetictesting
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Although the greatest contributors to #rheumatoid #arthritis (RA) heritability are the major histocompatibility complex (#MHC) proteins -encoded by the human leukocyte antigen (#HLA) region on chromosome 6-, 34 low-frequency and rare genetic variants have been associated with RA, including variants in #immune-related #genes such as #TYK2 that might represent therapeutic targets. 🔗https://lnkd.in/dSdVwhES
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