Meet the author of our latest whitepaper and discover how Scendea can support your FDA interactions when navigating the Rare Paediatric Disease Priority Review Voucher Program ahead of the September 2024 sunset deadline. - Read and download the whitepaper now -https://lnkd.in/g8SdRH9E - #whitepaper #drugdevelopment #regulatoryaffairs
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Great panel today on the ISPOR paediatric utilities task force. Please come and join me tomorrow at 10am for panel 315 The Invisible Costs in Rare Disease Management: Who Bears the Expense? We will be exploring the challenges facing the reimbursement assessment of rare disease from different perspectives. With Nicole Lyn , Michael Drummond and Daniel de Vicente. #ISPORAnnual
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Boost your clinical trial success with our on-demand webinar on building trust with rare disease patients and accelerating enrollment. This webinar is designed to unveil the essential strategies and practices for fostering trust among rare disease patients, which is pivotal in accelerating clinical trial enrollment. Watch now: https://lnkd.in/gqfzUh3D #ClinicalTrials #RareDiseases #PatientTrust
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Access + expertise can help #lifesciences meet enrollment goals for rare disease clinical trials. Join us at #DPHARM2024 to hear how.
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💫 FDA Approval 💫 🌟 Niktimvo™ (axatilimab-csfr) for the Treatment of Chronic Graft-Versus-Host Disease (GVHD) 👉 Pivotal data from the AGAVE-201 study supporting the approval show treatment with Niktimvo resulted in durable responses across all organs studied and patient subgroups 🔗 https://buff.ly/46QIWn7 #OncEd #OncoAlert
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Common variable immunodeficiency (CVID) is the most common clinically significant primary immunodeficiency disease (PID) and is known to manifest in both children and adults. With a prevalence of 1/10,000 to 1/50,000 in the Middle East, CVID remains a concern. Consanguineous marriages are common practice in the MENA region, and it is acknowledged that PIDs are more prevalent in areas with high rates of consanguineous marriages. To raise awareness of PID, CSL Behring urges for regular CVID screening to facilitate early diagnosis and timely medical intervention, before further damage occurs. #CSLBehring #MEA #RareDisease #DrivenbyOurPromise #CVID #PID #PrimaryImmunodeficieny
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Common variable immunodeficiency (CVID) is the most common clinically significant primary immunodeficiency disease (PID) and is known to manifest in both children and adults. With a prevalence of 1/10,000 to 1/50,000 in the Middle East, CVID remains a concern. Consanguineous marriages are common practice in the MENA region, and it is acknowledged that PIDs are more prevalent in areas with high rates of consanguineous marriages. To raise awareness of PID, CSL Behring urges for regular CVID screening to facilitate early diagnosis and timely medical intervention, before further damage occurs. #CSLBehring #MEA #RareDisease #DrivenbyOurPromise #CVID #PID #PrimaryImmunodeficieny
Common variable immunodeficiency (CVID) is the most common clinically significant primary immunodeficiency disease (PID) and is known to manifest in both children and adults. With a prevalence of 1/10,000 to 1/50,000 in the Middle East, CVID remains a concern. Consanguineous marriages are common practice in the MENA region, and it is acknowledged that PIDs are more prevalent in areas with high rates of consanguineous marriages. To raise awareness of PID, CSL Behring urges for regular CVID screening to facilitate early diagnosis and timely medical intervention, before further damage occurs. #CSLBehring #MEA #RareDisease #DrivenbyOurPromise #CVID #PID #PrimaryImmunodeficieny
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Let's raise awareness together! Common Variable Immunodeficiency (CVID) is the most common primary immunodeficiency disease in the Middle East. With a prevalence of 1/10,000 to 1/50,000, early screening is crucial! Let's make a difference in healthcare! #CVID #PID #immunodeficiency #raredisease #IworkforCSLBehring
Common variable immunodeficiency (CVID) is the most common clinically significant primary immunodeficiency disease (PID) and is known to manifest in both children and adults. With a prevalence of 1/10,000 to 1/50,000 in the Middle East, CVID remains a concern. Consanguineous marriages are common practice in the MENA region, and it is acknowledged that PIDs are more prevalent in areas with high rates of consanguineous marriages. To raise awareness of PID, CSL Behring urges for regular CVID screening to facilitate early diagnosis and timely medical intervention, before further damage occurs. #CSLBehring #MEA #RareDisease #DrivenbyOurPromise #CVID #PID #PrimaryImmunodeficieny
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At HI NENC we have developed tried and tested cardiovascular disease prevention resources, to support the spread of innovation and best practice in primary care. 💭 In this blog, hear from pharmacists from North Cumbria, Nicola Sumbler and Jennifer Nellis. The two pharmacists share their approach to lipid optimisation, to improve patient outcomes and support QOF targets. Read here ➡️ https://bit.ly/3vxLo3H #ZeroCVD #CVD
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Great to see the progress being made in the UK towards HCV elimination. NHS England is working to surpass the WHO target through a number of initiatives including a unique and innovative partnership – The Hepatitis C Elimination Programme which is a 7 year programme. Injecting drug use continues to be the biggest risk factor for HCV infection. Among those who inject drugs, or have previously injected, approximately 50% have HCV. HCV prevention strategies, including high coverage of needle and syringe programs, opioid agonist therapy, HCV screening and treatment, and addressing underlying barriers to service access, can dramatically reduce incidence toward elimination of HCV. #hepatitisC #harmreduction #publichealth #prevention #harmreductionsaveslives #nhs
MSD is delighted to extend our involvement in The Hepatitis C Elimination Programme, building on 5 years of success. Together, we're making significant progress to eliminate Hepatitis C and improving patient care in the UK 🙌 Read more about the programme https://lnkd.in/eMRmkkjd
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Unifying the name, definition, and diagnostic criteria of Pediatric Blepharokeratoconjunctvitis could help clinicians elude diagnostic confusion and detect the disease at early stages, avoiding sight-threatening complications. https://ja.ma/4ayJAr1
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