Solid Biosciences’ Post

Time is running out - register today! Clinical trials in #ophthalmology require special considerations at each stage, including trial design, recruitment strategies, patient outreach and much more. Success means putting patients and their caregivers first. Our panel of speakers will address advances in trial design specific to rare/genetic diseases of the eye, focusing on cell and gene therapy and the need to work collaboratively in this space. https://lnkd.in/epa4Ee_T #opthalmologyclinicaltrials #rarediseases #clinicaltrials #cellandgenetherapy

Join us in the webinar as we dive into how to conduct efficient trials in ophthalmology.

Clinical trials in #ophthalmology require special considerations at each stage, including trial design, recruitment strategies, patient outreach and much more. Success means putting patients and their caregivers first. Our panel of speakers will address advances in trial design specific to rare/genetic diseases of the eye, focusing on cell and gene therapy and the need to work collaboratively in this space. Register today. https://lnkd.in/epa4Ee_T #opthalmologyclinicaltrials #rarediseases #clinicaltrials #cellandgenetherapy

Planning a trial in an ophthalmology indication? --> I'd highly encourage taking a look at our webinar where our experts will share key considerations that will help facilitate successful study execution. 30 Jan @ 5pm CET

Only one week until the webinar! Clinical trials in #ophthalmology require special considerations at each stage, including trial design, recruitment strategies, patient outreach and much more. Success means putting patients and their caregivers first. Our panel of speakers will address advances in trial design specific to rare/genetic diseases of the eye, focusing on cell and gene therapy and the need to work collaboratively in this space. https://lnkd.in/epa4Ee_T #opthalmologyclinicaltrials #rarediseases #clinicaltrials #cellandgenetherapy

Tomorrow is the day! Clinical trials in #ophthalmology require special considerations at each stage, including trial design, recruitment strategies, patient outreach and much more. Success means putting patients and their caregivers first. Our panel of speakers will address advances in trial design specific to rare/genetic diseases of the eye, focusing on cell and gene therapy and the need to work collaboratively in this space. https://lnkd.in/epa4Ee_T #opthalmologyclinicaltrials #rarediseases #clinicaltrials #cellandgenetherapy

Exciting Day 2 of Advanced Therapies Week down in Miami! So far, we’ve had the privilege to connect with some of the leading innovators in the field of Cell & Gene Therapy, one of the youngest fields in science today that holds a lot of promise for the future tomorrow. Between learning about innovative drug delivery methods to actual patient saving cell replacement therapy, this field holds so much promise for a better tomorrow. We are excited to sync up innovative strategies for how #CGT can prevent the progression of type two to type three diabetes. Share your interesting ideas below! #MindfulDiabetes #JOINTHECAMINO

It was an absolute pleasure to attend and speak at the Gene Therapy Patient Engagement Summit again last week! A few takeaways: 📩 Direct and indirect engagement with the patient community should start even before the pre-clinical phase, as soon as a target condition has been identified   🤝 Early internal cross-functional alignment is critical to ensure patient advocacy is integrated into and considered in every functions' outputs   🏥 More consideration is needed when communicating the commitment of the long-term follow-up required post-gene therapy trials; for patients who have lived around hospital appointments and procedures for decades, we cannot underestimate the burden of having to continue this for a further 15 years    📺 When planning engagements and outreach to patients, it is critical to meet the communities where they're at

The blood-brain barrier (BBB) regulates molecule and ion movement between the circulation and the brain. In this webinar, Douglas Marchuk and Viviana Gradinaru will explain how new gene therapy approaches for combatting neurological disease overcome the BBB. Register now: https://ow.ly/acyG50Szau1

Check out the HCMS 2023 Sessions Abstract Publication in the Journal of Cardiac Failure that includes: 👉 Efficacy and safety of mavacamten treatment 👉 AAV9-Mediated Gene Therapy 👉 Characteristics of Patients in SEQUOIA-HCM 👉 & much more! https://lnkd.in/eNhx8kgn #HCM #Cardiology #CardioTwitter