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June 13th marks Rare Chromosome & Gene Disorder Awareness Day, a day which aims to raise awareness and encourage a greater understanding of rare chromosome and gene disorders amongst all.   Join us in raising awareness about the daily challenges faced by those affected, and their families, by unique genetic variations.   At #SpliceBio, we are focused on developing life-changing #genetherapies using our proprietary #ProteinSplicing platform which offers the potential to address diseases that currently cannot be treated with gene therapies, due to the necessary gene being too large to be delivered by adeno-associated virus (AAV) vectors.   Our lead program, SB007 targets #Stargardtdisease, a genetic eye disease that causes vision loss in children and adults. Stargardt disease is the most common inherited retinal disorder, affecting 1 in 8,000 to 10,000 people.   #biotech #retinaldiseases #lifesciences #genetherapy #rarechromoday #shinebrighttogether

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