Amylyx Pharmaceuticals' ALS drug, Relyvrio, didn't meet its goals in the crucial Phase III trial, casting uncertainty on its future. Despite this, the drug's safety profile remained consistent. Considerations - 🔹 The impact on ALS treatment advancements and patient hope. 🔹 Potential regulatory discussions and the commitment to patient well-being may guide Amylyx's next steps. This setback in ALS research emphasizes the challenges in neurodegenerative disease treatment but also the unwavering quest for solutions. #ALS #HealthcareNews #ClinicalTrials
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On May 9, 2024, the Centre for Pharmaceutical Medicine Research, King's College London hosted a ‘Spring 2024 Patient Engagement Workshop’. The multi-stakeholder workshop aimed to address challenges and seek ways to support evidence-based implementation of #patientengagement in medicines development and research. Here we summarize some of the key sessions that took place throughout the day. Read at The Evidence Base® #outcomesresearch #rwe #rwd #realworldevidence #realworlddata #regulation #regulatoryaffairs #hta #healthtechnologyassessment #healthdata #healthequity #healthpolicy
Multistakeholder perspectives on patient and public collaboration in medicines development: highlights of the spring 2024 patient engagement workshop
evidencebaseonline.com
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The interstitial cystitis drugs market is on a robust growth trajectory, projected to reach $1.67 billion by 2028. This expansion is fueled by increased attention to rare diseases, innovations in biopharmaceuticals, and regulatory support for orphan drugs. Key trends include advancements in diagnostics and the rise of targeted therapies, enhancing patient care and outcomes. Learn more about the interstitial cystitis drugs market: https://lnkd.in/g-5vF2ee . . . #interstitial #cystitis #drugs #medications #tbrc #thebusinessresearchcompany #marketresearch #marketintelligence
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Thoughts on this? >> FDA is poised to pull Ocaliva as adcomm documents question post-approval study results >> Comment below! >>> lqventures.com #strategy #competitiveintelligence #marketing #healthcare #biotech #pharma #productmarketing #pharmaceutical
FDA is poised to pull Ocaliva as adcomm documents question post-approval study results
endpts.com
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The average annual cost of treating a rare disease patient in the US is $32,000, with some cases exceeding $100,000. Treating rare diseases is challenging due to limited markets and high costs resulting from research and development investments. To address these issues, the industry is adopting a more sustainable approach driven by payer scrutiny and budget considerations. Pharmaceutical companies should employ these key strategies to maintain pricing and market access for rare disease therapies > https://owy.mn/4buhsp1 #OWHealth #RareDisease #Pharma
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Oliver Wyman's Health and Life Sciences Francois Lucas and Marc Tomassi identify four areas that pharmaceutical companies must examine to sustain attractive rare disease pricing and market access in this article > https://owy.mn/4buhsp1 #RareDiseases #OWHealth #Pharma
The average annual cost of treating a rare disease patient in the US is $32,000, with some cases exceeding $100,000. Treating rare diseases is challenging due to limited markets and high costs resulting from research and development investments. To address these issues, the industry is adopting a more sustainable approach driven by payer scrutiny and budget considerations. Pharmaceutical companies should employ these key strategies to maintain pricing and market access for rare disease therapies > https://owy.mn/4buhsp1 #OWHealth #RareDisease #Pharma
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BioPharma & HealthTech Competitive Strategy & Insights | Digital & AI Solutions | Gene & Cell Therapy | Vaccines
Thoughts on this? >> FDA is poised to pull Ocaliva as adcomm documents question post-approval study results >> Comment below! >>> lqventures.com #strategy #competitiveintelligence #marketing #pharmaceutical #productmarketing #pharma #biotech #healthcare
FDA is poised to pull Ocaliva as adcomm documents question post-approval study results
endpts.com
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Pivotal shifts in healthcare marketing demand we stay informed and agile. Hemogenyx Pharmaceuticals' recent update illustrates the strategic advancements in therapies for blood diseases, highlighting FDA movements and the upcoming Phase I trials for HEMO-CAR-T. The importance of partnerships in clinical settings, like MD Anderson, cannot be overstated. Let’s explore how these developments shape our marketing strategies and potential for growth in an evolving landscape. #HealthcareMarketing #PharmaInsights
Hemogenyx Pharmaceuticals PLC Announces Half-year Report
snip.ly
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Co-Founder ViTel Health *Champion for Independent Physician Practices and Equitable Care * Healthspan Optimization Physician with Rebel Health Alliance
Has anyone else noticed the concerning trend of pharmaceutical companies buying physicians? In telehealth, companies like Hims/Hers and Eli Lilly are employing doctors to prescribe their drugs. Now, we're witnessing pharmaceutical companies purchasing oncology practices to push chemotherapy drugs. It raises questions – physicians can't receive "kickbacks" for prescribing, yet pharma can control doctors to boost sales. Where does this cycle stop? If you're tired of your medical degree being exploited for others' gains, maybe it's time to rethink healthcare delivery. Let's return to a model where the physician and patient collaborate on treatment decisions – a return to what medicine should truly be. Read more about this issue here: [Link to article] #healthcare
Why Drug Distributors Are Buying Cancer Specialists
wsj.com
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More exciting news from my team!
We’re excited to share that AB-1005, which is being developed for moderate Parkinson’s disease, received US FDA Fast Track and UK MHRA Innovation Passport designations. There's a huge unmet need for #Parkinson's treatment, and these designations take us another step closer to accelerating access for patients. We at #AskBio, alongside Bayer | Pharmaceuticals, are dedicated to providing patients with innovative therapies and, most importantly, improving patient outcomes. #genetherapy For Medical Media – Read our press release here: https://lnkd.in/g7Mr854f
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Continued Emphasis on the Brain Disease Model: Despite its limitations, the brain disease model continues to dominate largely because it supports the development and funding of medical treatments and pharmaceutical interventions, which are concrete, scalable, and economically beneficial for the medical and pharmaceutical industries. Additionally, this model has played a significant role in shaping public policies and research agendas. #Addiction #Recovery
