PTC Therapeutics, Inc.

Sharing a great Key Account Manager role in Germany!

Today we announced that the U.S. Food and Drug Administration (FDA) has accepted for review the resubmission of the New Drug Application (NDA) for Translarna™ (ataluren) for the treatment of nonsense mutation Duchenne muscular dystrophy (nmDMD). Learn more: https://bit.ly/3A9hWDF

Delegates, patients and caregivers from across Europe are at the E.S.PKU Conference to discuss how to improve the quality of life of persons affected by phenylketonuria (PKU). To make traveling with #PKU easier, PTC is proud to support the launch of a new E.S.PKU metabolic passport which will be available to member organizations exclusively at the PTC exhibition booth. Meet Christian Frenzel and PTC colleagues to obtain a copy. We look forward to seeing you there! #ESPKU2024

Today we announced that we will host a conference call to report our third quarter 2024 financial results and provide an update on the company's business outlook on Thursday, Nov. 7 at 4:30 p.m. ET. Learn more: https://bit.ly/3A1InLv

October 23 is AADC Deficiency Awareness Day, an event aimed at promoting education about aromatic L-amino acid decarboxylase (AADC) deficiency. PTC is proud to help raise awareness about this rare, genetic disorder#AADCd. #AADCdAwarenessDay #aadcdeficiency #RareDiseaseAwareness

AADC (Aromatic L-Amino Acid Decarboxylase) Deficiency Awareness Day is coming up on October 23rd! This day is crucial for raising awareness about this rare genetic condition that affects the production of neurotransmitters like dopamine and serotonin, leading to severe developmental and neurological challenges. By spreading the word, we can help drive research, support families, and ensure earlier diagnoses. Let’s stand together with the AADC community and shine a light on the importance of advancing treatments and care. In light of this, I encourage everyone to read this insightful article, The Challenges of Early Diagnosis of AADC Deficiency. Early detection can significantly improve outcomes, yet many families face delays in diagnosis due to the rarity and complexity of symptoms. Raising awareness can change this! #AADCDeficiency #RareDiseaseAwareness #EarlyDiagnosis #October23 #HealthcareInnovation #Support #PTC #proudPTCemployee @ PTC Therapeutics, Inc.

This week we'll be onsite at the 18th International Congress on Neuromuscular Diseases (ICNMD 2024) in Perth, Australia. Be sure to stop by Booth 304 to meet our team. We invite all attending healthcare professionals to join us for our sponsored medical symposium on Sunday, Oct. 27. Register here: https://bit.ly/3Nzrw5B We look forward to seeing you there! #ICNMD2024 #DMD

We work to pioneer innovative treatments for patients around the world. As a part of these efforts, we are proud to share that our gene therapy for AADC deficiency has received regulatory approval for eligible patients in Brazil and Taiwan. #AADCd #genetherapy

PTC is proud to recognize #AADCDeficiencyAwarenessDay on Wednesday, Oct. 23. Join the AADC Family Network and special guests at 11 a.m. EDT to learn more about the condition and need for increased awareness. RSVP: https://bit.ly/3A3aXvK #AADCd #AADCdeficiency