PharmAust might just be that 1 in 1000 company! This morning, PharmAust CEO Michael Thurn shared some big news. They've begun giving doses in the Open Label Extension study to the 12 participants from the MEND #Phase1 trial for Motor Neurone Disease (#MND / #als ). In addition, they've revealed some key findings from #statisticalmodeling, which suggest a significant benefit in terms of survival. Simply put, if 12 similar MND patients were not treated at all, the chances of any of them surviving 12 months would be less than 0.1% or 1 in 1000. This analysis came from experts in statistics and PharmAust's partner, Berry Consultants, LLC. Looking at it another way, PharmAust has defied the odds as not one of the patients involved in their Phase 1 clinical trial for MND has passed away, some 15 months after the start of the clinical trial. The fact that all 12 patients have maintained their ability to swallow is a great data point. Statistically, there was a 99.9% chance at least one of the patients would NOT have survived 12 12-month Phase 1 clinical trial. To put this into context, a recently FDA-approved drug for ALS/MND, called RELYVRIO, showed a survival rate of around 75% in its 48-week trial. PharmAust has also informed the market that the Phase 1 Clinical Trial results are expected this quarter. This is an exciting moment where solid data may back up anecdotal evidence. From a recent roadshow presentation (below), there is a great graphic illustrating the typical progression of MND/ALS. The average survival time from diagnosis is approximately two years. The fact that all participants in PharmAust's MND Phase 1 trial can still swallow suggests, anecdotally, that there has been little decline in the group of 12 over the last 15 months. #biotechnology #motorneuronedisease #asxnews Roger Aston Sam Wright Robert C Bishop John Clark Blue Ocean Equities is the corporate advisor to PharmAust Limited Video Presentation to investors
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Did you know? LGC AXIO Proficiency Testing operates a wide range of clinical and forensic schemes and we continually increase our support for clinical laboratories and their External Quality Assessment (EQA) needs. Within clinical laboratories, testing requirements can often be within a narrow range, and the outcome of the tests is often critical for patient care. Likewise, within toxicological and forensic drug testing laboratories, matrices and drug metabolites can be challenging, with the outcome of the testing having potential legal repercussions. Our AXIO proficiency testing schemes are supported by Advisory Groups consisting of members of professional bodies and others experienced in the field. By participating in our schemes, laboratories can have confidence in the accuracy and quality of their tests. Explore more in our 2024 catalogue: https://okt.to/i3AZkl #DrivingQualityTogether #ForensicAnalysis #toxicology
LGC AXIO PT | Clinical & Forensic Tox Schemes 2024 Catalogue
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Introducing a new drug to market requires a complex interplay of multiple activities and disciplines. From #research and #development to clinical trials, regulatory #compliance, and manufacturing, the process can be challenging and time-consuming. In our latest video, Mark A. Lane - Vice President Development Consulting & #Scientific Affairs at PharmaLex, speaks on the importance of #IntegratedProductDevelopment in the #pharmaceutical industry. With his extensive experience and expertise, Mark highlights the various aspects that need to be considered in order to bring a new drug to market successfully and efficiently. 📽️ Watch the full video here: https://lnkd.in/erzypKUd
Pharmalex - Interviews Headquarters - Mark Highlight
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Life at a biotech is quite different from life in big pharma. Which one's right for you? Hear Orlando A. Granado-Balaez, DNP, MSL-BC's advice on how to make that decision on the latest episode of Pharma Sessions, now streaming everywhere.
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🎧 New Episode Alert! 🌟 Dive deep into the world of biosimilars with Pharmland. In the latest episode, hosts J Bradley Nelson and Thomas Davies explore the slow adoption of biosimilars in healthcare with Principal Advisor Ruth Opdycke. 🌿 Listen in as they discuss biosimilars’ potential to lower drug costs and the barriers limiting their widespread use. Don’t miss out on this insightful conversation! Streaming now: https://rxbene.fit/3zHojxr #PharmlandPodcast #Biosimilars #HealthcareCosts #PharmacyInnovation
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Great news on Kinpeygo!
European Commission extended approval of STADA's orphan drug | STADA
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Professor at The University of British Columbia, Editor in Chief Journal of Genetic Counseling
Another video of a talk I did recently! This one is from the 2023 World Congress on Genetic Counseling. It’s about establishing genetic counseling as a legitimate area of study with academic credibility- specifically, why that’s important and how we achieve it… I end up examining the definition and “central tenets” of genetic counseling and adding to them, so if any of these things is of interest, here’s the talk! https://lnkd.in/gcVK8SaX
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🎥 Our Sales Director Massimo Contri recently sat down with INTERPHEX Global TV to discuss a hot topic in the #pharmaceutical industry: #ArtificialIntelligence! At #BrevettiCEA, we believe that the transformative power of #AI in #healthcare it's not just about #innovation, it's about saving lives and ensuring safer #medicines for patients worldwide. 🔔 Don't miss out! Click the link below to watch the full #interview and gain valuable insights into the impact of AI in the #pharmaindustry. 💉🎬✨ #ArtificialIntelligence #HealthcareInnovation #automaticinspection #inspectionofparenteral #AllSaferMedicines https://lnkd.in/d2NbxdGc
INTERPHEX TV 2024 - Massimo Contri
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Renatus Inc., a pharmaceutical company developing cholesterol modulators for the treatment of cholesterol-driven diseases, was introduced on Pax Economy TV's 'Close-Up of Business', which introduces promising small businesses based in South Korea. Renatus’ proprietary cholesterol modulator, RN-005, has shown to promote cholesterol metabolism and mediate cholesterol efflux in varying disease models including chronic kidney disease and atherosclerosis, wherein cholesterol metabolism plays critical roles in their pathogenesis. It has successfully secured domestic and international patents for the drug candidate and its use for the treatment of cholesterol-driven diseases. Dysregulated cholesterol homeostasis and its accumulation is commonly observed in chronic kidney disease (CKD), which affects 1 in 8 adults worldwide. RN-005 treatment in CKD models demonstrated its renoprotective effects, as it significantly reduced blood creatinine, BUN levels and albuminuria. Renatus is preparing for a clinical trial for chronic kidney disease in both humans and companion animals. Heegon Kim, CEO of Renatus, commented: “To date, no medicine has been developed to normalize cholesterol metabolism and promote its efflux in our body. Our goal is to develop a safe and effective cholesterol modulator so that it can be used to treat various cholesterol-driven diseases including chronic kidney disease, and thereby improve the quality of life of the patients.” #Renatus #cyclodextrin #RN005 #cholesterolmodulator #interview #chronickidneydisease #animalhealth
RENATUS WAS INTRODUCED ON PAX ECONOMY TV
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Experience the benefits of BEMER in just 8 minutes, twice a day. Designed to stimulate muscles to temporarily increase local blood circulation in healthy muscles, BEMER devices have helped thousands of people improve their performance and recovery time. Find out more today! https://lnkd.in/drdyK7df And remember, you can try it out in our office! Let’s talk. These statements have not been evaluated by the FDA and this device is not intended to diagnose, treat, cure, or prevent any disease. Please consult your own physician or healthcare provider if you have any medical issues. #bemertherapy #bemergo #bemercommunity #bemerusa #bemerlife
What is BEMER in 8 Minutes (US, 2024)
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