TREAT-NMD

We regret to inform you that the TREAT-NMD 8th International Conference, originally scheduled for February 6th-8th, 2025, has been postponed due to the escalating situation in the Middle East.   The safety of our attendees is our top priority, and due to ongoing logistical concerns, we have made the necessary decision to delay the event.   We are working on securing new dates and locations. If you wish to be updated, please register your interest here > https://lnkd.in/e2vbyrtM we will communicate these details as soon as they are confirmed and let you know when tickets are available.   Thank you for your understanding and continued support!   Stay tuned for updates and follow us for more information.

There's just over 2 weeks until TREAT-NMD’s Developing Therapies in Rare Neuromuscular Diseases Symposium, marking 15 years of TACT. Whether you’re involved in clinical trials, regulatory affairs, or drug development for NMD, this symposium offers invaluable insights and practical strategies to support your work. Join us in Boston on 31st October for: −         Expert Insights: Learn from leading experts like Dr. Heather Gordish-Dressman and Dr. Conrad “Chris” Weihl on advanced trial design and therapeutic de-risking. −         Regulatory Insights: Engage with Dr. Pavel Balabanov (EMA) and Dr. Carl Peck (FDA) on navigating regulatory challenges. −         Interactive Q&A: Discuss with global leaders like Dr. Brian Tseng on managing ultrarare diseases. −         Networking Opportunities: Connect with industry leaders and peers to foster long-term collaboration. Don’t miss out, get your ticket today > https://lnkd.in/eADByJG5 #TACTSymposium #DrugDevelopment #ClinicalTrials #NeuromuscularDiseases #RareDiseaseResearch #RegulatoryAffairs #Biotech #PharmaInnovation #MedicalResearch #HealthcareLeadership #TherapeuticDevelopment

Muscular Dystrophy UK are hosting a 2024 virtual information seminar on Becker Muscular Dystrophy on Friday 18th October 2024 10am-12pm.    The BMD Hub will be represented by Abby Scott (BMD Hub Project Manager) and Prof. Michela Guglieri (Study Principal Investigator/Clinical Strand Lead). The session will explore the latest research on #BMD, along with information and guidance on living well with the condition.    For more information and to register: https://lnkd.in/ec9yfjmF

📢 Registration Open: TREAT-NMD Myotonic Dystrophy Type 1 (DM1) Expert Masterclass Registrations are now open for our virtual DM1 Expert Masterclass on 16th January 2025, chaired by Nicholas Johnson and Benedikt Schoser. This event is designed for healthcare providers involved in diagnosing and managing DM1. Gain the latest insights on diagnostic pathways, standards of care, and emerging therapies, while engaging with experts, patients, and peers to enhance DM1 care. Register now to secure your place by filling out the registration form here > https://lnkd.in/gXnk5di8 #TREATNMD #DM1Masterclass #HealthcareEducation

As we wrap up Becker Muscular Dystrophy Awareness Week, we want to thank everyone who shared their stories and supported the campaign. It's been an inspiring week hearing from individuals like David, Oriol, and Marc, and we are committed to continuing to raise awareness about Becker muscular dystrophy (BMD) throughout the year. For families and individuals affected by BMD, comprehensive Family Guides on the Diagnosis and Management of Becker muscular dystrophy are available to access via our website all year round. TREAT-NMD have recently facilitated the translation of this guide into additional languages to ensure even more families around the world can access essential information and support. You can explore the guides and find helpful resources here > https://lnkd.in/euU9t2YV #BMDawareness #BeckerMD #BeckerAwarenessWeek #BeckerMuscularDystrophy #MuscularDystrophyAwareness #Inform #Connect #Advance #TogetherWeAreStronger

Living with Becker muscular dystrophy – Oriol and Marc Following on from David Hick's story, we’re pleased to share the inspiring journey of Oriol and Marc, two brothers who are both living with Becker muscular dystrophy (BMD). "It was nice to share our story, and a privilege, we were happy to do that! As we grew up...we never had someone to look at and say: 'I want to be like him!' So we made our own journey." Despite their diagnosis, Oriol and Marc haven’t let BMD hold them back. They’re living their lives to the fullest, pursuing their passions and showing that BMD doesn’t define them. #BeckerAwarenessWeek #BMDawareness #BeckerMD #BeckerMuscularDystrophy #BMDJourney #LivingWithBMD #PatientStory #Inform #Connect #Advance #TogetherWeAreStronger

Living with Becker muscular dystrophy - Meet David Hick As part of Becker Muscular Dystrophy Awareness Week we’re highlighting the inspiring journeys of individuals living with BMD. David was diagnosed in July 2023, and his story is one of resilience and hope. What started with sudden pain while moving into his new flat led to months of tests, ending with a BMD diagnosis. David has since participated in clinical trials and uses his platform to raise awareness of BMD. Read his full story here > https://lnkd.in/e35tFph4 #BeckerAwarenessWeek #BMDawareness #BeckerMD #BeckerMuscularDystrophy #BMDJourney #LivingWithBMD #PatientStory #Inform #Connect #Advance #TogetherWeAreStronger

We’re proud to share highlights from our recent Becker Education and Engagement Days in Amsterdam and Milan. These events brought together individuals living with BMD, their families, and leading experts to connect, learn, and support one another. Read our latest blog for an overview of these incredible events and stay tuned as we share inspiring stories from some of the patients who attended— stories that raise awareness, offer hope, and show the strength of the BMD community > https://lnkd.in/eChrZCpm Special thanks again to Muscular Dystrophy UK, BMD Hub, AFM-Téléthon, Duchenne Parent Project Belgium, World Duchenne Organization, Parent Project aps, Duchenne Parent Project España and Deutsche Gesellschaft für Muskelkranke e.V. for their support with these events. #BEED #BeckerMD #BeckerMuscularDystrophy #Inform #Connect #Advance #TogetherWeAreStronger

It's Becker Muscular Dystrophy Awareness Week! (6th-12th October) This week, we shine a light on Becker muscular dystrophy (BMD), a rare genetic condition that causes a weakness in the muscles that progresses over time. Awareness weeks like this help raise understanding, but the need for support, education, and community continues year-round. At TREAT-NMD, we are committed to advancing the diagnosis, care, and treatment of BMD through ongoing efforts that inform, connect, and drive research forward. Read our latest blog to learn more about how we can build a more compassionate and supportive future for those affected by BMD: https://lnkd.in/eAYjD5F3 #BMDawareness #BeckerMD #BeckerAwarenessWeek #BeckerMuscularDystrophy #MuscularDystrophyAwareness #Inform #Connect #Advance #TogetherWeAreStronger

At WMS? Come and visit Cathy Turner at poster 689 to find out more about our Advisory Committee for Therapeutics!