ITF Therapeutics LLC

In our new blog, our team members will take turns providing updates, introducing themselves, sharing a more personal look at ITF Therapeutics, and highlighting information that we hope will be helpful for individuals and families navigating life with a rare disease, including Duchenne muscular dystrophy (DMD). We look forward to sharing a behind-the-scenes look at our work and inviting questions from the community. Check out our first entry from Caroline Allen, Head of US Patient Advocacy and Communications, to read her perspectives on today’s announcement about the availability of a therapeutic option for DMD: https://lnkd.in/gKjccDSK   #Duchenne #DMD #RareDiseases

We are excited to share that our therapeutic option for the treatment of Duchenne muscular dystrophy (DMD) is now commercially available in the U.S. For details, see our press release: https://lnkd.in/gNTPrN5M   Over the past several weeks, our entire team has worked closely with many members of the DMD advocacy and medical communities to bring this treatment option to people living with DMD as rapidly as possible. Thank you to all the families, advocates, and clinicians who supported this effort and helped make this historic milestone possible. We are also pleased to announce the launch of ITF ARC (Access, Resources and Care), a comprehensive program that includes services to help patients and families navigate through insurance challenges as well as personalized pharmacist support, financial and access assistance for eligible patients, educational materials, and other resources. The valued feedback and guidance that we received from DMD advocacy leaders helped shape ITF ARC at every stage of its development, and we are grateful for this opportunity to collaborate with the community.   #Duchenne #DMD #RareDiseases

Thank you to the Jett Foundation for hosting an engaging webinar with our VP, Medical Affairs Scott Baver, Ph.D., to share information about our work to advance a therapeutic option for DMD and provide an overview of the resources and services that we have developed to support people living with DMD and their families. Check out the webinar recording here: https://bit.ly/3Wo4mEq #Duchenne #DMD #RareDiseases

Durante casi una década, The Akari Foundation (Fundación Akari) ha desempeñado un papel fundamental a la hora de proporcionar a la comunidad hispana información y recursos importantes relacionados con la distrofia muscular de Duchenne (DMD) a través de iniciativas de concienciación y defensa que se esfuerzan por educar y capacitar a las personas que viven con DMD y a sus familias. Como nos unimos a la Fundación Akari en la celebración de su 7º aniversario este mes, estamos muy contentos de compartir que vamos a participar en un seminario web especial con la especialista neuromuscular Dra. Diana Castro, el viernes 19 de julio a las 10 a. m. ET para proporcionar información actualizada sobre nuestro trabajo para avanzar en una opción terapéutica para la DMD y hablar sobre el conjunto de servicios que hemos desarrollado para apoyar a las personas que viven con DMD y sus familias. ¡Esperamos verlo allí! Regístrese aquí: https://lnkd.in/esW29We2

For nearly a decade, The Akari Foundation has played a central role in providing the Hispanic community with important information and resources related to Duchenne muscular dystrophy (DMD) through awareness and advocacy initiatives that strive to educate and empower people living with DMD and their families. As we join The Akari Foundation in celebrating their 7th anniversary this month, we are excited to share that we will be participating in a special webinar with neuromuscular specialist Diana Castro, M.D., on Friday, July 19 at 10 a.m. ET to provide updates on our work to advance a therapeutic option for DMD and discuss the suite of services that we have developed to support individuals living with DMD and their families. We hope to see you there! Register here: https://lnkd.in/esW29We2 #Duchenne #DMD #RareDiseases

The “What Now?” virtual conference hosted by Team Joseph, a leading patient advocacy group serving the Duchenne muscular dystrophy (DMD) community, is a one-of-a-kind event that we are truly proud to support. With programming shaped by a planning committee including older adolescents and adults living with DMD, the meeting will share insights and perspectives to help navigate adulthood and prepare for the challenges and opportunities ahead for individuals living with DMD.   Learn more about this important event for the DMD community taking place virtually July 17-18 at 1-5 p.m. ET: https://lnkd.in/eMrhx3Nn   #Duchenne #DMD #RareDiseases

Our team was proud to join the Duchenne muscular dystrophy (DMD) community at Parent Project Muscular Dystrophy’s 30th Annual Conference! From our participation in the Patient Assistance Program sessions to our chats around the exhibit floor, we had the chance to hear from so many individuals living with DMD and their families about their personal experiences and hopes for the future. It was inspiring to see the community join together to show support, celebrate each other’s achievements, and learn about the latest advances in research. During the meeting, we also had the opportunity to participate in PPMD’s Duchenne Drug Development Roundtable and lead a focus group that provided invaluable insights on the needs and goals of the DMD community. In addition, our VP, Medical Affairs Scott Baver, Ph.D., delivered a special presentation to share information about our work to advance a therapeutic option for DMD and discuss the services that we have developed to support individuals living with DMD and their families. We are grateful to PPMD for hosting this important event and are honored to serve this resilient community. #Duchenne #DMD #RareDiseases

As we join with the Duchenne muscular dystrophy (DMD) community at the Parent Project Muscular Dystrophy’s 30th Annual Conference, our VP, Medical Affairs Scott Baver, Ph.D., will be delivering a presentation to share information about a therapeutic option for DMD and provide an overview of the resources and services that we have developed to support individuals living with DMD and their families. Check out the conference agenda for more details: https://lnkd.in/eJqUzYEf We are privileged to contribute to this event and look forward to engaging in meaningful discussions with members of the DMD community to help discover new opportunities to work together and make a positive impact. #Duchenne #DMD #RareDiseases

The Parent Project Muscular Dystrophy’s 30th Annual Conference not only facilitates education, connection, and inspiration within the Duchenne muscular dystrophy (DMD) community, but also provides an important platform to celebrate the strength of individuals living with DMD and their families. We are deeply honored to serve this resilient community and are excited to participate in this year’s event to actively learn from and engage with attendees who share our commitment to making a positive difference for people living with DMD. During the conference, our team will be available during the Patient Assistance Program 1:1 sessions being held Saturday, June 29 at 9:30 a.m. and 12 p.m. ET to share key updates on the resources and services that we have developed to support people living with DMD and their families. You can also find us at our booth on the exhibit floor – we hope to see you there! https://lnkd.in/exuJZnwq #Duchenne #DMD #RareDiseases

We have had the privilege to listen and learn from many outstanding members of the DMD community whose personal perspectives continue to shape and empower our work. Guided by the valued feedback that we have received from individuals living with DMD and their families, our team has been focused on developing a complete range of services designed to help meet their diverse needs and deliver new educational resources. We are excited to share that we will be participating in a special webinar with CureDuchenne on Wednesday, June 26 at 2-3 p.m. ET to provide updates on our support program and answer questions from the community. This virtual event is free to attend and open to the public – to join us, register here: https://lnkd.in/giQu5Whi #CureDuchenne #Duchenne #DMD #RareDiseases