Abeona Therapeutics’ Post

February 29 is Rare Disease Day. There are limited treatment options and cures for patients battling their rare disease. Take a moment to learn about a rare disease today!: Abeona Therapeutics, a clinical-stage biopharmaceutical company, is advancing gene-corrected epidermal sheets to treat recessive dystrophic epidermolysis bullosa. This genetic skin disorder makes the skin fragile and susceptible to chronic wounds. The Ataxia Telangiectasia Children's Project works to find therapies and a cure for children with Ataxia-telangiectasia, a genetic disease that impairs muscle control and the immune system. #rarediseaseday2024

On this rarest of dates, IQVIA celebrates #RareDiseaseDay by publishing our latest blog on how #RealWorldEvidence can improve our understanding and evaluate the effectiveness of new therapies for rare diseases.

🔔Have a look to this scientific session🔔: TRL IS COSTLY: THE VALUE OF ELUVIA DES AN ENDOVASCULAR APPROACH IN FEM-POP DISEASE With unrestricted support of Boston Scientific #toracicaorta #abdominalaorta #peripheralarterialdisease #endoavf #dialysisistula #criticalallimbischemia #abdominalaorta

Learn how #AI-driven quantitative CT analysis methods increase precision in evaluating #LungFibrosis on #HRCT images, including stratifying baseline disease severity and assessing response to therapy in #ClinicalTrials. https://lnkd.in/giQ86WYY #MedicalImaging #ArtificialIntelligence #Pulmonary #ChooseCalyx

Learn how #AI-driven quantitative CT analysis methods increase precision in evaluating #LungFibrosis on #HRCT images, including stratifying baseline disease severity and assessing response to therapy in #ClinicalTrials. https://lnkd.in/gBvqbNvk #MedicalImaging #ArtificialIntelligence #Pulmonary #ChooseCalyx

Today we recognize #RareDiseaseDay which turns our attention to the 300 million patients who suffer from #rarediseases globally. The goal of Rare Disease Day is to work towards #equity for people living with a rare disease. We turn our focus to this important cause today to highlight this vulnerable population. In an effort to connect the world with the right doctors, H1 has 700,000 #HCPs, globally, focused on treating rare disease patients and putting efforts toward testing new rare disease treatments to keep these patients top of mind. The insights shared here comes from our internal data to show the scale of the impact that rare diseases have across the globe. #healthequity #dei #raredisease

AL #amyloidosis is a rare, progressive, and often fatal disease. There is an urgent unmet need for therapies that address both the toxic, circulating amyloid and the amyloid deposited in vital organs for those living with AL amyloidosis. Learn more about our work in this area by visiting our pipeline: https://bit.ly/3x06KXT #AmyloidosisAwarenessMonth

In this consecutive, all-comers cohort, disease complexity was associated with procedural selection and MALE-FS. AVB independently provided the greatest MALE-FS and freedom from MALE and major amputation. Compared to the BEST-CLI randomized trial, MALE after ENDO in this series was more frequently major amputation, with relatively few conversions to open bypass.

Learn how #AI-driven quantitative CT analysis methods increase precision in evaluating #LungFibrosis on #HRCT images, including stratifying baseline disease severity and assessing response to therapy in #ClinicalTrials. https://lnkd.in/gcgNfyEf #MedicalImaging #ArtificialIntelligence #Pulmonary #ChooseCalyx

Understanding the #molecularpathways of #medicalconditions is crucial for developing #targetedtherapies and #personalizedmedicine. By identifying the specific #molecularmechanisms involved in a disease, researchers can design more effective treatments that address the root cause of the condition. #molecularmedicine #precisionmedicine